PTC Therapeutics Receives Positive CHMP Opinion for Upstaza™ for the Treatment of AADC Deficiency
- Friday, May 20, 2022, 7:14
- Business
- Add a comment
– First ever gene therapy directly administered into the brain – – Recommended for regulatory approval by EMA – – Results demonstrated sustained improvements in motor and cognitive function – – Conference call scheduled for Monday, May 23, at 8 a.m. ET – SOUTH PLAINFIELD, N.J., May 20,…